orphan drug

基本解釋

Objective: To introduce American Orphan Drug System.
目的：介紹美國罕見病藥物制度。
A drug is eligible for orphan drug designation if it is intended to treat a disease or condition that affects less than 200,000 people in the United States.
當一種疾病影響小于20萬美國人時，治療該疾病的藥品被指定為稀少藥品。
Orphan drug designation is available for drugs already approved for another disease or condition or for experimental drugs that have not been previously approved.
已經(jīng)被批準用于其它疾病治療的藥物或者是尚處于試驗階段未被批準的藥物都可以通過孤兒藥物申報程序進行。

Without the Orphan Drug Act, there would probably be no Biogen Idec, no Genzyme, Alexion Pharmaceuticals.
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One idea is to create an incentive for drugmakers comparable to that in the Orphan Drug Act.
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AZT, began as an orphan drug for what was then an obscure disease of the immune system.
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